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Tackling Analytical Challenges in Gene Therapy

Key considerations on how to navigate the field as a gene therapy developer. In 2017, the U.S. FDA approved the first gene therapy after decades of hope, setbacks, and finally success. Several others have since been approved and dozens more are in pivotal trials, cementing this targeted approach as a viable treatment option for a range of genetic disorders. These therapies can potentially be a one-time treatment, furthering expanding their potential.